Gene Therapy

Neurodegenerative Disease Insights Can Advance Precision Medicine

by Erin McNemar, MPA

Rutgers researchers discovered some of the first molecular insights into how toxic proteins are regulated in neurodegenerative disease, potentially advancing precision medicine efforts. The most...

How Proteins in Acute Myeloid Leukemia Support Precision Medicine

by Erin McNemar, MPA

Sanford Burnham Prebys Medical Discovery Institute scientists discovered that the protein RNF5 plays an unusual role in acute myeloid leukemia (AML). By targeting the specific protein, researchers...

Why Genetic Testing Is Key to Advancing Precision Medicine

by Erin McNemar, MPA

Due to genetics, not every patient responds the same to medications. With genetic testing, providers can better determine the best treatment options for individuals, advancing precision...

Improving Cancer Treatment, Patient Outcomes with Genomic Testing

by Erin McNemar, MPA

New York University (NYU) is using a new kind of genomic testing to improve cancer treatment and patient outcomes. Cancer has proven to be difficult to manage for patients and healthcare providers....

Addressing Cardiovascular Genetic Testing in Children

by Erin McNemar, MPA

According to a new statement from the American Heart Association, cardiovascular genetic testing in children presents challenges that require pre-and post-test counseling with a personalized approach...

Neurological Disease Study Leads to Precision Medicine Progress

by Erin McNemar, MPA

A new study from the University of Arizona Health Sciences could lead to a breakthrough in the development of precision medicine to prevent neurodegenerative diseases. By studying women on hormone...

Gene Therapy Improves Neurological Disease, Population Health Management

by Erin McNemar, MPA

A study led by researchers at The Ohio State University Wexner Medical Center and The Ohio State University College of Medicine shows that a new method of gene therapy is providing...

Mayo Clinic Uses Genomics to Understand Neurodevelopmental Disorders

by Erin McNemar, MPA

Researchers at Mayo Clinic have found genetic variants in SPTBN1, a neuro-associated gene, are the reason behind neurodevelopmental disorders. This application of genomics is the first step in...

CRISPR Shows Promise in Gene-Editing Therapy During Clinical Trial

by Erin McNemar, MPA

Scientists at UCL National Amyloidosis Centre at the Royal Free Hospital, London are hoping their gene editing therapy using CRISPR will be a breakthrough for patients suffering from hereditary...

Precision Medicine Therapy Restores Immune Function in Children

by Jessica Kent

A precision medicine therapy developed by researchers at UCLA and Great Ormond Street Hospital (GOSH) in London restored immune function in more than 95 percent of pediatric patients. Using the...

Gene Therapy Preserves Memory in Alzheimer’s Mouse Model

by Jessica Kent

A team from University of California San Diego School of Medicine has leveraged gene therapy to preserve learning and memory in a mouse model of Alzheimer’s, indicating that the approach could...

$10.7M Grant Will Support Study of Genomic Data in Alzheimer’s

by Jessica Kent

The University of Pittsburgh Graduate School of Public Health and Washington University School of Medicine in St. Louis will lead a five-year, $10.7 million project that will explore the role of...

Routine Genetic Testing May Impact Patient Outcomes, Survival

by Jessica Kent

Many cardiomyopathies in children are the result of genetic mutations, making a strong case for routine genetic testing to improve patient outcomes, according to a study published in the Journal of the...

Precision Medicine Therapy Improves Congenital Blindness

by Jessica Kent

In an initial clinical trial, researchers found that a new precision medicine therapy for a common form of congenital blindness was safe and improved patients’ vision, according to a study...

Clinical Trial Will Evaluate Gene Therapy for Alzheimer’s Disease

by Jessica Kent

A team from UC San Diego School of Medicine will conduct a clinical trial to assess the value of a gene therapy to deliver a protein into the brains of people with Alzheimer’s disease. The...

Genomic Data Advances Precision Medicine for Prostate Cancer

by Jessica Kent

As disease treatments continue to advance and become more personalized, researchers are increasingly relying on genomic data to accelerate the development of precision medicine for a range of...

UCLA Uses $29M Gift to Establish Precision Medicine Center

by Jessica Kent

UCLA has received a $29 million gift to establish a precision medicine center where scientists can leverage big data and genomic technologies to improve genetic disease treatment and diagnosis. The...

Precision Medicine Platform Aims to Advance Cancer Gene Therapies

by Jessica Kent

A team from Cleveland Clinic has developed a precision medicine platform designed to accelerate cancer gene therapies and genome-informed drug discovery. In a study published in Nature Genetics,...

Genetic Database May Enable Precision Medicine for COVID-19

by Jessica Kent

Researchers from the University of Alabama at Birmingham have created a genetic database designed to help advance precision medicine treatments for COVID-19. The database, called PAGER-CoV-2, includes...

Gene Involved in Breast Cancer Growth May Speed Precision Medicine

by Jessica Kent

A team from UT Southwestern (UTSW) has found that a significant number of breast cancer patients have higher levels of the ZMYND8 gene, making it a potential target for immunotherapies and precision...